Genome Editing in Neurosciences

Genome Editing in Neurosciences

Jaenisch, Rudolf; Zhang, Feng; Gage, Fred

Springer International Publishing AG

08/2018

123

Mole

Inglês

9783319868011

15 a 20 dias

454

Descrição não disponível.
Introduction.- In vitro modeling of complex neurological diseases.- Aquatic model organisms in neurosciences : the genome editing revolution.- Genome-wide genetic screening in the mammalian CNS.- CRISPR/Cas9-mediated Knockin and Knockout in Zebrafish.- Dissecting the role of synaptic proteins with CRISPR.- Recurrently Breaking Genes in Neural Progenitors: Potential Roles of DNA Breaks in Neuronal Function, Degeneration and Cancer.- Neuroscience research using non-human primate models and genome editing.- Multiscale genome engineering: Genome-wide screens and targeted approaches.- Using Genome Engineering to Understand Huntington's Disease.- Therapeutic gene editing in muscles and muscle stem cells.
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CRISPR-Cas9;genetic engineering;recombinant-DNA methods;double-strand breaks;Ciona intestinalis;isogenic IPSCs;Parkinson's disease;Huntington's disease;Rett syndrome;Duchenne muscular dystrophy;Open Access